澳洲幸运5开奖号码历史查询

Rocket Pharmaceuticals Stock Craters After Gene Therapy Patient Dies

Rocket Pharma
The news sent shares of Rocket Pharmaceuticals plungi꧃ng to an all-time🅠 low.

Rocket Pharma

Key Takeaways

  • Rocket Pharmaceuticals halted a study of a gene-therapy drug for Danon disease because a patient had a "Serious Adverse Event" and later died.
  • The patient suffered from complications related to a blood vessel leak.
  • The news sent shares of Rocket Pharmaceuticals plunging to an all-time low.

Rocket Pharmaceuticals (RCKT) shares plunged to an all-time low Tuesday when the drugmaker reported a patient taking its experimental treatment for Danon disease had a "Serious Adverse Event (SAE)" and later died, putting a halt to the research.

The company explained that in a 澳洲幸运5开奖号码历史查询:Phase 2 trial of its investigational gene therapy RP-A501, the patient experienced "clinical complications related to a capillary leak s♔yndrome," and subseqﷺuently "passed away after an acute systemic infection."

Rocket Pharmaceuticals said it is conducting a "comprehensive root cause analysis" that is currently focusing on "the recent introduction of a novel immune suppression agent to the pre-treatment regimen that had been implemented to mitigate complement activation observed in some patients."

After the incident, Rocket Pharmaceuticals paused the study, and the 澳洲幸运5开奖号码历史查询:Food and Drug Administration (FDA) placed a clinical hold on it. The company⛎ said it "is unable to provide guidance on the anticipated timing for completion of the Phasꦬe 2 trial."

Shares of Rocket Pharmaceuticals lost 60% their value in Tuesday morning trading, and are down about 80% year-to-date. 

RCKT

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